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Patients with cystic fibrosis who could not receive the CFTR modulator treatment: What did they lose in 1 year?

Salih UytunGuzin CinelSanem Eryılmaz PolatSatı Özkan TabakçıNural KiperEbru YalçınDilber Ademhan TuralBeste ÖzsezenVelat ŞenHadice Selimoğlu ŞenDerya Ufuk AltıntaşHaluk ÇokuğraşAyse Ayzit KilincAzer Kılıç BaşkanHakan YazanAbdulhamit ÇollakSelçuk UzunerGökçen ÜnalAsli Imran YilmazHanife Tuğçe ÇağlarEbru Damadoğluİlim IrmakEsen DemirGökçen Kartal ÖztürkAyşen BingölAbdurrahman Erdem BaşaranNihat SapanYakup CanıtezAyşe Tana AslanPelin AsfuroğluKoray HarmancıMehmet KöseMelih HangulAli OzdemirNazan CobanogluGizem ÖzcanÖzlem KeskinHasan YükselŞebnem ÖzdoğanErdem TopalGönül ÇaltepeDemet CanPervin Korkmaz EkrenMehmet KılıçNagehan EmiralioğluTugba Sismanlar EyubogluSevgi PekcanErkan CakirUğur ÖzçelikDeniz Dogru Ersoz
Published in: Pediatric pulmonology (2023)
Patients who had indications for modulator treatments but were unable to obtain them worsened even after a year of follow-up. This study emphasized the importance of using modulator treatments for patients with CF in our country, as well as in many countries worldwide.
Keyphrases
  • cystic fibrosis
  • pseudomonas aeruginosa
  • lung function