Early indicators of disease progression in Fabry disease that may indicate the need for disease-specific treatment initiation: findings from the opinion-based PREDICT-FD modified Delphi consensus initiative.
Derralynn A HughesPatricio AguiarPatrick B DeeganFatih EzguAndrea FrustaciOlivier LidoveAleš LinhartJean-Claude LubandaJames C MoonKathleen NichollsDau-Ming NiuAlbina NowakUma RamaswamiRicardo ReisinPaula RozenfeldRaphael SchiffmannEinar SvarstadMark ThomasRoser TorraBojan VujkovacDavid G WarnockMichael L WestJack JohnsonMark J RolfeSandro FeriozziPublished in: BMJ open (2020)
PREDICT-FD captured global opinion regarding current clinical indicators that could prompt FD-specific treatment initiation earlier than is currently practised.