Treatment Strategies for Deficiency of Adenosine Deaminase 2.
Amanda K OmbrelloJing QinPatrycja M HoffmannParag KumarDeborah StoneAnne JonesTina RomeoBeverly BarhamGineth Pinto-PatarroyoCamilo ToroAriane SoldatosQing ZhouNatalie DeuitchIvona AksentijevichSherry L SheldonSusan KellyAda ManKaryl BarronMichael HershfieldWilly Albert FlegelDaniel L KastnerPublished in: The New England journal of medicine (2019)