The French Compassionate Program of elexacaftor-tezacaftor-ivacaftor in people with cystic fibrosis with advanced lung disease and no F508del CFTR variant.
Pierre Regis BurgelIsabelle Sermet-GaudelusIsabelle DurieuReem KanaanJulie MaceyDominique GrenetMichele PorzioNathalie Coolen-AllouRaphael ChironChristophe MarguetBenoit DouvryNadine DufeuIsabelle Danner-BoucherPierre FoucaudLydie LemonnierEmmanuelle GirodonJennifer Da SilvaClémance Martinnull nullPublished in: The European respiratory journal (2023)
variants not currently approved for ETI.