Health-related quality of life in patients with β-thalassemia: Data from the phase 3 BELIEVE trial of luspatercept.
Maria Domenica CappelliniAli T TaherAntonio PigaFarrukh ShahErsi VoskaridouVip ViprakasitJohn B PorterOlivier HermineEllis J NeufeldAlexis A ThompsonDerek TangAylin YucelJennifer Lord-BessenPeiwen YuShien GuoJeevan K ShettyDimana MitevaTatiana ZingerJay T BackstromEsther Natalie OlivaPublished in: European journal of haematology (2023)
Luspatercept + BSC reduced transfusion burden while maintaining patients' HRQoL. HRQoL domain improvements from baseline through 48 weeks were also enhanced for luspatercept responders.