Login / Signup

Health-related quality of life in patients with β-thalassemia: Data from the phase 3 BELIEVE trial of luspatercept.

Maria Domenica CappelliniAli T TaherAntonio PigaFarrukh ShahErsi VoskaridouVip ViprakasitJohn B PorterOlivier HermineEllis J NeufeldAlexis A ThompsonDerek TangAylin YucelJennifer Lord-BessenPeiwen YuShien GuoJeevan K ShettyDimana MitevaTatiana ZingerJay T BackstromEsther Natalie Oliva
Published in: European journal of haematology (2023)
Luspatercept + BSC reduced transfusion burden while maintaining patients' HRQoL. HRQoL domain improvements from baseline through 48 weeks were also enhanced for luspatercept responders.
Keyphrases
  • end stage renal disease
  • newly diagnosed
  • ejection fraction
  • chronic kidney disease
  • sickle cell disease
  • clinical trial
  • peritoneal dialysis
  • cardiac surgery
  • phase iii
  • machine learning
  • phase ii
  • artificial intelligence