Development and Validation of a Patient-Reported Outcome Measure of Ataxia.

Jeremy D SchmahmannSamantha PierceJason MacMoreGilbert J L'Italien

Published in: Movement disorders : official journal of the Movement Disorder Society (2021)

The Patient-Reported Outcome Measure of Ataxia is valid and reliable in cerebellar ataxia patients. It has the potential to improve patient care and natural history studies and quantify the efficacy of novel therapeutics in clinical trials. © 2021 International Parkinson and Movement Disorder Society.

Keyphrases

patient reported outcomes
clinical trial
early onset
ejection fraction
small molecule
newly diagnosed
prognostic factors
risk assessment