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Cystic fibrosis transmembrane conductance regulator modulator administration to a F508del heterozygous infant with meconium pseudocyst and short bowel syndrome: A case report.

Sylvia StoffellaNgoc LyMeghan E McGarryFatima NeemuchwalaGwynne ChurchMarilynn ChanAddison CuneoMakiko OmoriElizabeth Gibb
Published in: Pediatric pulmonology (2023)
Keyphrases
  • cystic fibrosis
  • pseudomonas aeruginosa
  • early onset
  • lung function
  • transcription factor
  • case report
  • air pollution
  • chronic obstructive pulmonary disease