Liver transplantation: New treatment for mucopolysaccharidosis type VI in rats.
Sumika ToyamaOhsuke MigitaMasayuki FujinoTetsuo KuniedaMotomichi KosugaYasuyuki FukuharaYukitoshi NagaharaXiao-Kang LiTorayuki OkuyamaPublished in: Pediatrics international : official journal of the Japan Pediatric Society (2019)
LTx from normal to affected MPR was effective for symptoms of MPS and accumulation of GAG, suggesting that LTx could be a promising alternative approach for MPS VI.