Nusinersen in adults with type 3 spinal muscular atrophy: long-term outcomes on motor and respiratory function.

Catarina Serrão Sara Domingues Catarina Falcão Campos Susana Moreira Isabel Conceição Mamede de Carvalho Miguel Oliveira Santos

Published in: Neurological sciences : official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology (2024)

Our cohort supports a sustained benefit of nusinersen in adults with type 3 SMA, in motor and respiratory function. Multicentric studies are still warranted.

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