RNA expression profiling in lymphoblastoid cell lines from mutated and non-mutated amyotrophic lateral sclerosis patients.
Jessica GarauMaria GarofaloFrancesca DragoniEveljn ScarianRosalinda Di GerlandoLuca DiamantiSusanna ZuccaMatteo BordoniOrietta PansarasaStella GagliardiPublished in: The journal of gene medicine (2024)
We conclude that LCLs are a good model for the study of RNA deregulation in ALS.