Login / Signup

Diagnosis and treatment of a boy with IPEX syndrome presenting with diabetes in early infancy.

Sejal KadakiaLauge FarnaesDavid DimmockShimul ChowdhuryYan DingEric J AndersonStephen KingsmoreRon S Newfield
Published in: Clinical case reports (2019)
IPEX syndrome (Immune dysregulation, Polyendocrinopathy, X-linked) should be tested for in males under 6 months old presenting with diabetes, even without other IPEX features. Early diagnosis and bone marrow transplantation can improve outcomes.
Keyphrases
  • case report
  • bone marrow
  • type diabetes
  • glycemic control
  • cardiovascular disease
  • mesenchymal stem cells
  • stem cells
  • weight gain
  • physical activity
  • adipose tissue
  • skeletal muscle
  • weight loss