Healthcare resource utilisation and direct medical cost for individuals with 5q spinal muscular atrophy in Sweden.
Thomas SejersenSophie GrahamAnne-Berit EkströmAnna-Karin KroksmarkMarta KwiatkowskaMichael L GanzNahila JustoKarl GertowAlex SimpsonPublished in: The European journal of health economics : HEPAC : health economics in prevention and care (2024)
The economic burden attributable to SMA is significant. Further research is needed to understand the burden in other European countries and the impact of new treatments.