Healthcare utilisation in children with SMA type 1 treated with nusinersen: a single centre retrospective review.

Imran Ali Francis J GilchristWilliam D CarrollJohn AlexanderSadie ClaytonRicha KulshresthaTracey WillisMartin P Samuels

Published in: BMJ paediatrics open (2019)

Patients with SMA1 treated with nusinersen initially spend a considerable proportion of their early life in hospital. Parents should be counselled accordingly. These data suggest that for every 10 children started on nusinersen an extra HDU bed is required. This has a significant cost implication.

Keyphrases

early life
healthcare
young adults
electronic health record
newly diagnosed
machine learning
social media