Refractory, fatal autoimmune hemolytic anemia due to ineffective thymic-derived T-cell reconstitution following allogeneic hematopoietic cell transplantation for hypomorphic RAG1 deficiency.
Jennifer R YonkofAmrita BasuMargaret T RedmondAdam Kerry DobbsLudmila PerelyginaLuigi D NotarangeloRoshini S AbrahamHemalatha G RangarajanPublished in: Pediatric blood & cancer (2022)