High-throughput screening identifies modulators of sarcospan that stabilize muscle cells and exhibit activity in the mouse model of Duchenne muscular dystrophy.
Cynthia ShuLiubov ParfenovaEkaterina MokhonovaJudd R ColladoRobert DamoiseauxJesus CampagnaVarghese JohnRachelle H CrosbiePublished in: Skeletal muscle (2020)
This study identifies a pharmacological approach to treat DMD and sets the path for the development of SSPN-based therapies.