Ruxolitinib for treatment of refractory hemophagocytic lymphohistiocytosis.
Larisa BroglieLauren PommertSridhar RaoMonica ThakarRachel PhelanDavid MargolisJulie TalanoPublished in: Blood advances (2017)
Optimal salvage therapy for refractory HLH is unknown.In our patient, ruxolitinib treatment led to clinical remission of refractory HLH.