Salbutamol repurposing ameliorates neuromuscular junction defects and muscle atrophy in Col6a1 -/- mouse model of collagen VI-related myopathies.
Sonia CalabròLeonardo NogaraYongzhi JianManuel ValentinDario BizzottoPaola BraghettaLoris RussoLisa GambarottoBert BlaauwSaid HashemolhosseiniPaolo BonaldoMatilde CesconPublished in: Clinical and translational medicine (2024)