Gene therapy: principles, challenges and use in clinical practice.

Cihan AyAndreas Reinisch

Published in: Wiener klinische Wochenschrift (2024)

Gene therapy holds great promise for considerable improvement or even cure of genetic diseases with serious clinical consequences. However, a number of questions and issues need to be clarified to ensure broad accessibility of safe and efficacious products.

Keyphrases

gene therapy
clinical practice
genome wide
big data
copy number
gene expression
deep learning
artificial intelligence