Emicizumab Dosing in Children and Adults with Hemophilia A: Simulating a User-Friendly and Cost-Efficient Regimen.
Laura H BukkemsKathelijn FischerIdske Kremer-HovingaAnouk A M DonnersKarin FijnvandraatRoger E G SchutgensMarjon H CnossenRon A A MathôtPublished in: Thrombosis and haemostasis (2021)
This alternative maintenance dosing scheme-applicable in patients with hemophilia A receiving emicizumab prophylaxis-reduces financial costs, avoids medication spillage, and is patient-friendly without loss of efficacy.