Development and Validation of the Pediatric Charcot-Marie-Tooth Disease Quality of Life Outcome Measure.
Sindhu RamchandrenTong Tong WuRichard S FinkelCarly E SiskindShawna M E FeelyJoshua BurnsMary M ReillyTimothy EstilowMichael E Shynull nullPublished in: Annals of neurology (2020)
The pCMT-QOL patient-reported outcome measure is a reliable, valid, and sensitive measure of health-related QOL for children with CMT. ANN NEUROL 2021;89:369-379.