Mesoporous Silica-Based Nanoparticles as Non-Viral Gene Delivery Platform for Treating Retinitis Pigmentosa.
Lourdes Valdés-SánchezSara Borrego-GonzálezAdoración Montero-SánchezSimone MassaliniBerta de la CerdaAránzazu Díaz-CuencaFrancisco J Díaz-CorralesPublished in: Journal of clinical medicine (2022)
N-MSiNPs are safe for retinal delivery and thus a potential alternative to viral vectors.