KW-2449 and VPA exert therapeutic effects on human neurons and cerebral organoids derived from MECP2-null hESCs.
Ya-Jie XuPei-Pei LiuZhong-Ze YanTing-Wei MiYing-Ying WangQian LiZhao-Qian TengChang-Mei LiuPublished in: Stem cell research & therapy (2022)
These findings suggest that KW-2449 and VPA might be promising drugs for RTT treatment.