Efficacy and safety of low-dose Sirolimus in Lymphangioleiomyomatosis.
Hee-Young YoonJung Jin HwangDong Soon KimJin Woo SongPublished in: Orphanet journal of rare diseases (2018)
Low-dose sirolimus may stabilise lung function decline in lymphangioleiomyomatosis patients, but its efficacy appears to be inferior to that of conventional-dose sirolimus.