Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party.
Su Han LumMilen MinkovSimon A JonesSheree HazelaarTiarlan SiraitJane E PotterPolina StepenskyFrederic GarbanHerbert PichlerJerry SteinZuhre KayaAnsgar S SchulzKarin MellgrenChristina Diaz de HerediaCecile PochonSusana RiescoMiguel Angel DiazGerard MichelCaroline LindemansBernd GruhnMichael H AlbertArjan C LankesterBénédicte NevenRobert F WynnPublished in: Bone marrow transplantation (2023)