Novel approaches to analysis of the North Star Ambulatory Assessment (NSAA) in Duchenne muscular dystrophy (DMD): Observations from a phase 2 trial.
Francesco MuntoniMichela GuglieriJean K MahKathryn R WagnerJohn F BrandsemaRussell J ButterfieldCraig M McDonaldAnna G MayhewJeffrey P PalmerShannon MarraffinoLawrence CharnasEugenio MercuriPublished in: PloS one (2022)
NCT02310763.