Efficacy, Safety and Quality of Life of Pegcetacoplan in Japanese Patients With Paroxysmal Nocturnal Hemoglobinuria Treated Within the Phase 3 PEGASUS Trial.
Hisakazu NishimoriHideyuki NakazawaShinobu TamuraToshiki UchidaKensuke UsukiJohan SzamosiRégis Peffault de LatourAlexander RöthJens PansePublished in: Acta haematologica (2024)
gov identifier: NCT03500549.