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Highly efficient bi-allelic correction of homozygous COL7A1 mutation using ABE8e adenine base editor.

Imogen R BrooksYara AlrokhAidin KazemizadehKatarzyna BalonGregory NewbyDavid R LiuŁukasz ŁaczmańskiJohn A McGrathJoanna Jackow-Malinowska
Published in: The British journal of dermatology (2023)
Keyphrases
  • highly efficient