Developing therapies for rare tumors: opportunities, challenges and progress.
Diana BradfordKarlyne M ReillyBrigitte C WidemannAbby SandlerShivaani Kummar
Published in: Expert opinion on orphan drugs (2015)
Future progress in developing therapies for rare tumors will depend not only on continued scientific advances, but also on collaboration between investigators from various disciplines, institutions, regulatory agencies and patient advocacy groups.