Repurposing eflornithine to treat a patient with a rare ODC1 gain-of-function variant disease.
Surender RajasekaranCaleb P BuppMara Leimanis-LaurensAnkit ShuklaChristopher RussellJoseph JunewickEmily GleasonElizabeth A VanSickleYvonne EdgerlyBryan M WittmannJeremy W ProkopAndré S BachmannPublished in: eLife (2021)
No external funding was received for this work.
Keyphrases