Real-world data of in-hospital administration of alglucosidase alfa in French patients with Pompe disease: results from the National Claims Database.
Shahram AttarianEmmanuelle Salort CampanaStanislas PerrierMarion AfonsoPierre KaramNassima HaiPascal LaforetPublished in: Journal of neurology (2024)
The analysis of the French hospital discharge database indicated that Myozyme® was associated with a low incidence of AEs and complications in a hospital context, supporting the consideration of its safe use in home-infusion settings.