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Molecular Evaluation and Vector Integration Analysis of HCC Complicating AAV Gene Therapy for Hemophilia B.

Manfred SchmidtGraham R FosterMichiel CoppensHauke ThomsenRicardo DolmetschLiesbeth HeijinkPaul E MonahanSteven W Pipe
Published in: Blood advances (2023)
Keyphrases
  • copy number
  • genome wide
  • genome wide identification
  • gene therapy
  • dna methylation
  • genome wide analysis