mNIS+7 and lower limb function in inotersen treatment of hereditary transthyretin-mediated amyloidosis.
P James B DyckJohn C KincaidJanice F WiesmanMichael PolydefkisWilliam J LitchyMichelle L MauermannElizabeth J AckermannSpencer GuthrieMichael PollockShiangtung W JungBrenda F BakerPeter J DyckPublished in: Muscle & nerve (2020)
The results of this analysis reinforce the beneficial effect of inotersen on slowing neuropathy progression in patients with hATTR polyneuropathy.
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