Acceptability of prenatal diagnosis and prenatal treatment of haemophilia using cell and gene therapies within US haemophilia community.
Quan D M PhamSharon M ThomsonBurk N SchaibleKevin D MillsAnthony AtalaChristopher D PoradaGraca Almeida-PoradaPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2023)
These data demonstrate the willingness of persons with haemophilia, and the haemophilia community, to explore new treatment options beyond the currently offered approaches.