Combination Therapy with Nusinersen and Onasemnogene Abeparvovec-xioi in Spinal Muscular Atrophy Type I.
Andrada MireaElena-Silvia ShelbyMihaela AxenteMihaela BadinaLiliana PadureMadalina LeancaVlad DimaCorina SporeaPublished in: Journal of clinical medicine (2021)
Our results suggest that early treatment is more important than combined therapy.
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