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Congenital pure red cell anemia and idiopathic very early onset of severe colitis cured by allogeneic hematopoetic stem cell transplantation.

Karin Baekgaard NissenTania Nicole MasmasRasmus Gaardskaer NielsenMette ChristiansenMarcin WlodarskiHenrik Hasle
Published in: Pediatric blood & cancer (2023)
Keyphrases
  • stem cell transplantation
  • early onset
  • high dose
  • late onset
  • single cell
  • chronic kidney disease
  • cell therapy
  • iron deficiency
  • mesenchymal stem cells
  • ulcerative colitis
  • bone marrow