A simple core dataset and disease severity score for hereditary transthyretin (ATTRv) amyloidosis.
Thibaud DamyIsabel ConceiçãoPablo García-PavíaJulian David GillmoreRavi JandhyalaJan SabbatJonas WixnerTeresa CoelhoPublished in: Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis (2021)
The resulting CD and DSS have different purposes. The ATTRv CD supports the collection of high-quality data for clinical research, whereas the ATTRv DSS can be rapidly conducted in a clinical setting and aid patient management.