Nusinersen for older patients with spinal muscular atrophy: A real-world clinical setting experience.

Aravindhan VeerapandiyanKaty EichingerDebra GuntrumJennifer KwonLindsay BakerErin CollinsEmma Ciafaloni

Published in: Muscle & nerve (2019)

Intrathecal nusinersen can be safely delivered in older SMA patients. Available functional outcome measures are not adequate to capture meaningful subjective improvements.

Keyphrases

end stage renal disease
chronic kidney disease
physical activity
newly diagnosed
ejection fraction
middle aged
community dwelling
peritoneal dialysis
prognostic factors
patient reported outcomes