Significant healthcare burden and life cost of spinal muscular atrophy: real-world data.

Sophelia Hoi Shan ChanCarlos K H WongTingting WuWilfred WongMichael K L YuIvan C H AuGodfrey C F Chan

Published in: The European journal of health economics : HEPAC : health economics in prevention and care (2022)

Our results confirmed a significantly raised mortality and extremely high healthcare burden for patients with SMA especially SMA type 1 and 2 without disease-modifying treatment. Study evaluating health and economic impact of newborn screening and early treatment is needed.

Keyphrases

healthcare
public health
risk factors
type diabetes
health information
risk assessment
big data