Miracle of haemophilia drugs: Personal views about a few main players.
Pier Mannuccio MannucciPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2018)
Current miraculous progress in hemophilia therapy is stemming from the research work of outstanding scientist physicians who acted in close collaboration with small biotechnology companies, leading to the early development of innovative therapeutic products, subsequently taken to the market place by the so called Big Pharma. I shall briefly provide my views to explain the fact that large pharmaceutical companies show more and more interest in such a rare disease as the hemophilias.