Nusinersen for Spinal Muscular Atrophy Type I with Chronic Respiratory Failure: A Retrospective Study in South Korea.

Hui Jin Shin Ji-Hoon Na Hyun Joo Lee Young Mock Lee

Published in: Yonsei medical journal (2023)

Nusinersen is safe and effective in patients with SMA type I, even those with chronic respiratory failure and those on permanent ventilation. No significant adverse effects of nusinersen were observed.

Keyphrases

respiratory failure
extracorporeal membrane oxygenation
mechanical ventilation
acute respiratory distress syndrome
emergency department
adverse drug