A Delphi panel to build consensus on assessing disease severity and disease progression in adult patients with hypophosphatasia in the United States.
Kathryn McCrystal DahirEric T RushS Diaz-MendozaP S KishnaniPublished in: Journal of endocrinological investigation (2024)
These statements regarding disease severity, progression, and assessment methods address some knowledge gaps in adult patients with HPP and may be helpful for treating HCPs, although the small sample size affects the ability to generalize the healthcare provider experience.