Pattern of use and clinical outcomes with rIX-FP in pediatric/adolescent patients with haemophilia B in Italy: Results from IDEAL real-world study.

Paola Giordano Berardino Pollio Gianluca Sottilotta Chiara BiasoliFilomena DanieleRaimondo De Cristofaro Flora PeyvandiMaria Rosaria VillaGiancarlo Castamannull null

Published in: European journal of haematology (2024)

The results in this pediatric/adolescent subgroup support rIX-FP prophylaxis may reduce infusion frequency, while providing high FIX trough levels, stable annualized bleeding rate and a good safety profile.

Keyphrases

young adults
mental health
childhood cancer
low dose
study protocol