Analysis of Structural Variants Previously Associated With ALS in Europeans Highlights Genomic Architectural Differences in Africans.
Nomakhosazana R MonnakgotlaAmokelani C MahunguJeannine M HeckmannGerrit BothaNicola M MulderGang WuEvadnie RampersaudJason MyersMarka Van BlitterswijkRosa RademakersJ Paul TaylorJoanne WuuMichael BenatarMelissa NelPublished in: Neurology. Genetics (2023)
gene therapy for related diseases such as spinal muscular atrophy.