A triple-blinded crossover study to evaluate the short-term safety of sweet manioc starch for the treatment of glycogen storage disease type Ia.
Vaneisse C L MonteiroBibiana M de OliveiraBruna B Dos SantosFernanda Sperb-LudwigLilia F RefoscoTatiele NalinTerry G J DerksCarolina F Moura de SouzaIda Vanessa Döederlein SchwartzPublished in: Orphanet journal of rare diseases (2021)
SMS appears to be non-inferior to UCCS in the maintenance of euglycemia, thus emerging as a promising alternative to the treatment of GSD Ia.
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