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Author Correction: Therapeutic manipulation of IKBKAP mis-splicing with a small molecule to cure familial dysautonomia.

Masahiko AjiroTomonari AwayaYoung Jin KimKei IidaMasatsugu DenawaNobuo TanakaRyo KurosawaShingo MatsushimaSaiko ShibataTetsunori SakamotoLorenz StuderAdrian R KrainerMasatoshi Hagiwara
Published in: Nature communications (2021)
Keyphrases
  • small molecule
  • protein protein
  • early onset