Amifampridine safety and efficacy in spinal muscular atrophy ambulatory patients: a randomized, placebo-controlled, crossover phase 2 trial.
Silvia BonannoRiccardo GiossiRiccardo ZaninValentina PorcelliClaudio IannaconeGiovanni BaranelloGary IngenitoStanley IyaduraiZorica StevicStojan PericLorenzo MaggiPublished in: Journal of neurology (2022)
NCT03781479; EUDRACT 2017-004,600-22.