Health-related quality of life and caregiver burden of emicizumab in children with haemophilia A and factor VIII inhibitors-Results from the HAVEN 2 study.
Maria Elisa MancusoJohnny N MahlanguRobert SidonioPeter TraskMarianne UguenTiffany ChangMidori ShimaGuy Aaron YoungJohannes OldenburgSylvia von MackensenPublished in: Haemophilia : the official journal of the World Federation of Hemophilia (2020)
Prophylactic emicizumab is accompanied by substantial and sustained improvements in HRQoL of paediatric PwHA with FVIII inhibitors and their caregivers.