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Tracking disease progression non-invasively in Duchenne and Becker muscular dystrophies.

Pietro SpitaliKristina HettneRoula TsonakaMohammed CharroutJanneke van den BergenZaïda KoeksHermien E KanMelissa T HooijmansAndreas RoosVolker StraubFrancesco MuntoniCristina Al-Khalili-SzigyartoMarleen J A Koel-SimmelinkCharlotte E TeunissenHanns LochmüllerErik H NiksAnnemieke Aartsma-Rus
Published in: Journal of cachexia, sarcopenia and muscle (2018)
Serum proteomic analysis allowed to not only discriminate among DMD, BMD, and healthy subjects, but it enabled to detect significant associations with clinical function, dystrophin levels, and disease progression.
Keyphrases
  • muscular dystrophy
  • duchenne muscular dystrophy
  • resistance training
  • body composition
  • high intensity