Safety and efficacy of mitapivat, an oral pyruvate kinase activator, in sickle cell disease: A phase 2, open-label study.
Myrthe J van DijkMinke A E RabBrigitte A van OirschotJennifer BosCleo DerichsAnita W RijneveldMarjon H CnossenErfan NurBart J BiemondMarije BartelsJudith J M JansWouter W van SolingeRoger E G SchutgensRichard van WijkEduard J van BeersPublished in: American journal of hematology (2022)