A new step in understanding stem cell mobilization in patients with Fanconi anemia: A bridge to gene therapy.

Jean-Sébastien DianaSandra ManceauThierry LeblancAlessandra MagnaniElisa MagrinMatthieu BendavidChloe CouzinLaure JosephJean SoulierMarina CavazzanaFrancois Lefrère

Published in: Transfusion (2021)

Our data in patients with FA show that the mobilization of HSCs with G-CSF and plerixafor is safe and more efficient in younger individuals without BMF.

Keyphrases

gene therapy
stem cells
electronic health record
chronic kidney disease
big data
iron deficiency
cerebrospinal fluid
mesenchymal stem cells
cell therapy
data analysis
bone marrow